Proximal spinal muscular atrophy type 3

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Proximal spinal muscular atrophy type 3

ORPHA:83419Clinical subtype

Also called Juvenile spinal muscular atrophy · Kugelberg-Welander disease · SMA type 3 · SMA type III · SMA-III · SMA3

What it is

A rare genetic motor neuron disorder characterized by degeneration of alpha motor neurons in the spinal cord and lower brainstem manifesting between 18 months and 18 years of age and associated with slowly progressive, predominantly proximal muscle weakness. By definition, individuals with proximal spinal muscular atrophy (SMA) type 3 achieve independent ambulation before symptom onset, but ambulation may be lost over the course of the disease.

Key facts

Prevalence
1-9 / 1 000 000 (Europe)
Age of onset
Adolescent, Adult, Childhood, Infancy
Inheritance
Autosomal recessive
Classified as
Clinical subtype

Prevalence figures describe populations, not individuals, and are often estimates from a single study. Where the figure is an incidence or a birth prevalence, it says so.

Genes

SMN1Disease-causing germline mutation(s)

2 modifying genes — variants that can change how the disease behaves, not cause it

NAIPSMN2

ICD-10 codes

G12.1filed under a broader ICD-10 category — shared with 15 other rare diseases

ICD-10 has no distinct code for most rare diseases, so many are filed under the nearest available one. A shared code identifies the group, not this disease — the ORPHAcode above is what identifies it.

Related health topics

Reached through the ICD-10 categories this disease is filed under, so these describe the broader group rather than this disease specifically.

Benefit programs to look at

Programs whose eligibility touches the same ICD-10 categories. Eligibility is decided by the administering agency, never by this page.

Cross-references

GARD 198MONDO 0009672OMIM 253400UMLS C0152109

Orphadata Science: Free access data from Orphanet. © INSERM 1999. Data version 2026-06-23. Available under CC BY 4.0. This is a reference, not medical advice.

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