Perrault syndrome type 2

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Perrault syndrome type 2

ORPHA:642976Clinical subtype

Also called XX gonadal dysgenesis-deafness syndrome-progressive neurological manifestations

What it is

A form of Perrault syndrome characterized by sensorineural, generally bilateral, prelingual, progressive and sometimes asymmetric hearing loss, primary ovarian dysgenesis in females and neurological features of variable severity including cerebellar dysfunction/athrophy with ataxia, intellectual disability, neuropathy and behavioral symptoms. Additional clinical features may involve developmental delay, muscular and renal manifestations.

Key facts

Inheritance
Autosomal recessive
Classified as
Clinical subtype

Recorded for the broader condition

Prevalence
<1 / 1 000 000Perrault syndrome
Age of onset
Adolescent, Adult, ChildhoodPerrault syndrome

Orphanet records these for the broader condition rather than for this specific form. They are a starting point, not a figure for this subtype — subtypes often differ, and some are defined by being rarer than the condition they sit under.

Genes

CLPPDisease-causing germline mutation(s)
ERAL1Disease-causing germline mutation(s)
GGPS1Disease-causing germline mutation(s)
HARS2Disease-causing germline mutation(s)
HSD17B4Disease-causing germline mutation(s)
LARS2Disease-causing germline mutation(s)
PRORPDisease-causing germline mutation(s) (loss of function)
RMND1Disease-causing germline mutation(s)
TWNKDisease-causing germline mutation(s)

Cross-references

MONDO 0013972UMLS C5816795

Orphadata Science: Free access data from Orphanet. © INSERM 1999. Data version 2026-06-23. Available under CC BY 4.0. This is a reference, not medical advice.

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